The first gene therapies approved to treat sickle cell disease in December 2023 are struggling on the market. But there are glimpses of forward momentum as Vertex and Genetix Bio provide updates.

“It can hit you out of nowhere,” she tells TODAY.com.

BUFFALO, N.Y. (WIVB) — Local groups are raising awareness about sickle cell disease and encouraging people to roll up their sleeves and donate blood. Sickle cell disease is a genetic blood disorder ...

Right now, approximately 20 billion red blood cells are busy traveling through your blood vessels. They are delivering oxygen to all the different tissues in your body and removing carbon dioxide to ...

CRISPR gene therapy Casgevy can nearly eliminate sickle cell crises, but difficult stem‑cell collection is delaying access ...

As Uganda rolls out mandatory nationwide screening of newborns for sickle cell disease this month, a gene therapy celebrated ...

This article is part of a Rare Disease series sponsored by DeepIntent. With Rare Disease Month wrapping up and Rare Disease Day taking place on Saturday, MM+M is celebrating a handful of campaigns ...

You Look Fine” is a groundbreaking new documentary, offering an intimate, first-person account of living with sickle cell disease.

Sickle cell anemia (SCA) is an inherited disorder of red blood cells. Some parents may learn that their infant has this disorder after prenatal testing. Hospitals also test for SCA after birth as part ...

Rare antigens found in the blood of those with African descent make it necessary even more for sickle cell patients.

"The shutting down of units like this, adding to people's waiting time, adding to people's journey time, are the types of things that could definitely leave someone with sickle cell in a lot of pain, ...

An Alberta father is advocating for a legislation that would create national policies for fighting against sickle cell disease after his son died nearly four years ago. Jacob Marfo, director of Ezra ...